Axsome Therapeutics, Inc. (NASDAQ: AXSM) uses its chiral chemistry and formulation capabilities to identify, isolate and stabilize chirally pure enantiomers for developing drug candidates for the treatment of central nervous system (CNS) disorders with large unmet needs. Its proprietary MoSEIC™ technology can increase the solubility...
Enlivex Therapeutics (NASDAQ: ENLV), a Company focused on developing allogenic therapies for immune system rebalancing, announced positive interim efficacy data from its ongoing Phase Ib clinical trial in patients with severe sepsis. The analysis in based on data collated from 43 patients with severe sepsis,...
Adverum Biotechnologies (NASDAQ: ADVM), a clinical-stage Company focused on developing therapeutics for ocular and rare diseases through gene therapy, released additional clinical data from its ongoing OPTIC phase 1 clinical trial of ADVM-022. ADVM-022, the Company’s lead ocular candidate, is an adeno- associated virus (AAV)....
Otonomy Inc (NASDAQ: OTIC), a biopharmaceutical company focussed on providing neurotology solutions, announced a strategic collaboration with Applied Genetic Technologies Corporation (NASDAQ: AGTC), a biotechnology company developing adeno-associated virus (AAV)-based gene therapies for the treatment of rare diseases, to create, develop and commercialize an AAV-based...
Nonalcoholic Steatohepatitis (NASH) is a form of Non-Alcoholic Fatty Liver Disease (NAFLD) and is characterized by the buildup of FAT in the liver. This condition is marked by hepatitis, inflammation, cell damage and fat deposits in the liver. These fat deposits can cause fibrosis of...
Rosacea affects over 415 million people worldwide, and more than 16 million in the U.S alone, according to research conducted by the University of Copenhagen, Denmark. It is a fairly common skin disorder, but only 18 percent of Americans afflicted with this condition are under...
Migraine is a genetic predisposition to moderate-to-severe headaches caused due to stress, physiological factors such as lack of sleep, hunger and environmental triggers such as sensitivity to lights and sounds or hormonal changes in case of women. It manifests in the form of throbbing pain...
The Muscular Dystrophy Association describes Duchenne Muscular Dystrophy (DMD) as a fatal, X-linked genetic neuromuscular disorder that leads to progressive, irreversible loss of muscle function, including the heart and lungs. It has an X-linked recessive inheritance pattern and is acquired by a “Carrier” mother. Globally, 1 in...
